Exploring clinical trials for Duchenne muscular dystrophy

If your child has Duchenne, there may be clinical trial options to explore, depending on age, genetic mutation, and medical history. Duchenne clinical trials can be mutation-specific and may have requirements related to walking ability, current medications (like steroids), or heart and lung health[Lm1.1]. A short call with a navigator can help you understand which clinical trial options may be relevant for your child’s situation and what may be worth keeping an eye on as new clinical trials open.

It depends on what feels manageable for your family, such as how your child is doing today, how much time and travel you could take on, and whether you want to explore options now or simply stay informed. A navigator can help you understand what exploring clinical trial options could involve and help you prepare questions to discuss with your child’s specialist. You can explore options without committing to anything, and you decide what happens next

You’ll speak with a navigator who will ask a few questions about your child’s diagnosis and current care, so we can understand what clinical trial options might be relevant. If you have genetic results, it helps to share them—but you don’t need everything ready to start. After the call, we’ll explain what options may be a match (if any) and what next steps could look like, including what you could discuss with your child’s specialist. You choose what happens next, and we won’t contact any clinical trial team without your permission.

Booking a call is not a commitment to joining a clinical trial. Many families speak with a navigator simply to understand what clinical trial options may exist and what joining a clinical trial could involve—even if they’re not ready to take part right now. After the call, you can decide what (if anything) you want to do next, including just staying informed. If you ever choose to move forward, that would only happen after speaking with your child’s doctor and the clinical trial team at the trial site, who can give you the full details of the trial. You decide if and when you want to explore any next step.[L

That can happen and it’s common. Duchenne clinical trials may have specific requirements related to age, mutation type, walking ability, current treatments, or heart and lung health[Lm1.1]. If your child isn’t eligible right now, your navigator can explain why, help you understand what to watch for, and keep you informed as new clinical trials open [Lm2.1][Rv2.2][Lm2.3]or criteria change. You can still use the call to get clarity and plan your next steps with your child’s specialist.

Not necessarily, but genetic results are often helpful, because many Duchenne clinical trials are mutation-specific. If you already have results, you can share them during or after the call. If you don’t, your navigator can explain why mutation information matters and what to discuss with your child’s care team to get the right details. Either way, you can still speak with a navigator to understand what options may exist now and what to keep an eye on for the future. We’ll only share information with a clinical trial team if you ask us to.

Sometimes, yes. Many Duchenne clinical trials take place at specialized hospitals, and joining a trial may require in-person visits for tests and check-ups. How much travel is needed depends on the specific clinical trial—some have sites in multiple regions, while others are only available in a few locations. Your navigator can help you understand what joining a clinical trial could involve, including where sites are located and what the visit schedule may look like. If you’re interested in a specific option, the clinical trial team can confirm practical details, including any travel support.

No, there’s no cost to speak with a myTomorrows patient navigator. The call is for information and guidance, so you can understand what clinical trial options may be relevant and what next steps could look like. You can decide what (if anything) you want to do after the call. You can take the information and decide what feels right for your family.

Yes. We handle any medical information you share securely and use it only to assess whether clinical trial options may be relevant. We will not share your information with any clinical trial team or hospital without your clear permission. You can ask questions, choose what you want to share, and decide what happens next.